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Biomolecules | Free Full-Text | Epigenetic Insights and Potential Modifiers as Therapeutic Targets in β–Thalassemia
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Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)
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Cureus | Improving Ineffective Erythropoiesis in Thalassemia: A Hope on the Horizon
Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)
β-Thalassemia | Genetics in Medicine
IJMS | Free Full-Text | Non-Transfusion-Dependent Thalassemia: An Update on Complications and Management
Full article: Revisiting beta thalassemia intermedia: past, present, and future prospects
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Sirolimus for Treatment of β-Thalassemia: From Pre-Clinical Studies to the Design of Clinical Trials
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Gene Therapy For Beta-Thalassemia: Updated Perspectives | TACG
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
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PDF) Selecting β-thalassemia Patients for Gene Therapy: A Decision-making Algorithm
JCM | Free Full-Text | Does Hepcidin Tuning Have a Role among Emerging Treatments for Thalassemia?
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
Safety and efficacy of thalidomide in patients with transfusion-dependent β- thalassemia: a randomized clinical trial | Signal Transduction and Targeted Therapy
Diseases | Free Full-Text | Luspatercept: A New Tool for the Treatment of Anemia Related to β-Thalassemia, Myelodysplastic Syndromes and Primary Myelofibrosis
Frontiers | The Future of Gene Therapy for Transfusion-Dependent Beta- Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells
Replacing the suppressed hormone: toward a better treatment for iron overload in β-thalassemia major? | Haematologica
